ProjectsClinical Study Protocols Clinical Study Reports (CSRs) ClinicalTrials.gov Postings Development Safety Update Reports (DSURs) FDA Briefing Packages Investigator's Brochures (IBs) Patient Safety Narratives Regulatory Submission Dossiers in eCTD Format including: BLAs, INDs, NDAs, MAAs Abstracts Posters Manuscripts |
Therapeutic IndicationsAdvanced Fibrosis Anemia Atopic Dermatitis Bacterial Endocarditis Breast Cancer Chemotherapy-induced Nausea and Vomiting Cholangiocarcinoma Chronic Obstructive Pulmonary Disease (COPD) Ebola Virus Familial Hypercholesterolemia Gastrointestinal Stromal Tumors Hematologic Neoplasms Lymphomas Lysosomal Acid Lipase Deficiency Mast Cell Leukemia Mycobacterium avium complex (MAC) Lung Disease Nontuberculous mycobacteria (NTM) Lung Disease Osteoporosis Pancreatic Cancer Platinum Sensitive Ovarian Cancer Primary Myelofibrosis Relapsed or Refractory Acute Myeloid Leukemia Solid Tumors Transthyretin-mediated Amyloidosis |